Areas of Interest – EMEA / APAC / LATAM
Please select a disease area to review all detailed information.
Friedreich Ataxia (FA)
- Educate healthcare professionals (HCPs) on early symptom recognition, diagnosis of FA, differential diagnoses, and the role of genetic counseling and testing.
- Improve patient and caregiver understanding of the disease and available care strategies.
- Increase HCP awareness of current guidelines for managing patients with FA.
- Provide education on managing cardiac and systemic complications associated with FA.
- Expand knowledge on managing patients with FA, including how coordinated, continuous care plans support adherence and showcase effective team‑based care models.
- Increase HCP understanding of how age of onset influences disease progression, including tools used across clinical disciplines to assess severity and the importance of proactive management for all patients.
- Enhancing healthcare professional understanding of multidisciplinary care approaches, disease progression expectations, appropriate assessment methods, and real‑world treatment adherence.
- Supporting the education of healthcare professionals on applying mFARS (Friedreich Ataxia Rating Scale) for the Assessment and rating of Ataxia, and Activities of Daily Living (ADL) measures to track and assess disease progression.
SMA
- Educate HCPs on the importance of biomarkers for tracking disease progression and monitoring treatment impact.
- Support HCP education on treatment strategies.
- Improve patient and caregiver understanding of the disease and available care approaches.